None Too Rare

Seeking the fastest path to discovery of therapies for rare and orphan genetic diseases regardless of prevalence.

How can you know you’re putting your gene
therapy on the best path to patients?

Are you in a long waiting
list for AAV?
Are you nervous
about cost?
Do you need cGMP material?
Are you anxious about
study delays?
Contact us

We're changing the way orphan drugs are discovered

"Current technology that could be used to treat many rare genetic diseases is held back by slow infrastructure. We're building the tools to power the next thousand cures."

Omid Karkouti, MSFounder and CEO, Perception Bio
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Our Investors